How A Doctor Helped A Young Patient With Fatal Disorder Defy Odds TODAY 5:05 2 years ago 4 683 Скачать Далее
2019 FAST Science Summit on Angelman Syndrome - Keynote, Dr. Emil Kakkis, Ultragenyx Pharmaceutical FAST 51:08 4 years ago 1 152 Скачать Далее
Emil Kakkis : Master of Ceremonies EveryLife Foundation for Rare Diseases 2:35 8 years ago 345 Скачать Далее
Learnings Guiding Clinical Trial Design for Heterogenous Populations Dr Emil Kakkis 2020 FAST FAST 25:02 3 years ago 162 Скачать Далее
Bay Area Creative Foundation: Founder, Dr. Emil Kakkis on Creativity Bay Area Creative Foundation 6:20 1 year ago 400 Скачать Далее
Faster Rare Disease Progress is Within our Reach with Dr. Emil Kakkis and Mary Woolley ResearchAmerica 16:40 2 years ago 203 Скачать Далее
Emil Kakkis - keynote lecture: Translating rare disease research into medicine Wellcome Connecting Science Learning and Training 37:08 2 years ago 418 Скачать Далее
Time for an Ultra-Orphan Drug Act by Dr. Emil Kakkis Cure GM1 Foundation 29:28 10 months ago 197 Скачать Далее
Developing Novel Treatments for Rare Disorders: A Look at MPS I with Dr. Emil Kakkis WCG 19:30 1 month ago No Скачать Далее
Bay Area Creative Foundation: Meet our Founder, Dr. Emil Kakkis Bay Area Creative Foundation 1:38 2 years ago 104 Скачать Далее
Wait, How Do You Spell That: A Rare Disease Podcast - Dr. Emil Kakkis, Founder of Ultragenyx Patient Worthy 25:13 5 months ago 23 Скачать Далее
Translational Medicine Symposium 2013: Dr. Emil Kakkis, 3 of 4 Albert Einstein College of Medicine 36:34 10 years ago 709 Скачать Далее
FDA Approval of Crysvita® for X-linked Hypophosphatemia (XLH) HPR 7:05 6 years ago 2 463 Скачать Далее
Ultragenyx CEO talks the company's path to profitability in developing drugs for rare diseases CNBC Television 3:38 7 months ago 755 Скачать Далее
Emil Kakkis, MD, PhD | The Challenges of Managing Heterogeneity in Rare Diseases EveryLife Foundation for Rare Diseases 23:54 5 years ago 408 Скачать Далее